Accueil - Vivet Therapeutics
Description: The Gateway Wilson Disease Clinical Trial is sponsored by Vivet Therapeutics and is accepting application enrollment. Check for Eligibility Now.
children (10136) mma (1591) trial (809) clinical (758) methylmalonic acidemia (1)
What you need to know about GATEWAY, a clinical trial for patients with Wilson Disease:
Wilson Disease is a rare genetic disorder that causes excess copper to build up in the body, particularly in the liver and brain. The disease is caused by mutations in a gene called ATP7B. If Wilson Disease is not diagnosed early and appropriately treated, the build-up of copper may cause serious damage to organs and result in severe disability and possibly death. This means that early diagnosis and prompt treatment is very important.
Although there are currently available medical treatments for Wilson Disease, patients need to take them for life and the therapeutic response is not optimal in some patients; therefore new therapeutic options are desirable.
Accueil - Vivet Therapeutics